Pompe Disease Treatment Market Research Report – Global Forecast till 2025 Highlights
The Global Pompe Disease Treatment Market is estimated to be valued at USD 1,414.1 million by 2025 and is expected to register a CAGR of 2.6% during the forecast period.
Global Pompe Disease Treatment Market: Information by Type (Late-Onset Pompe Disease, Classic Infantile-Onset Pompe Disease, Non-Classic Infantile-Onset Pompe Disease), by Therapy (Enzyme Replacement Therapy (ERT) and Gene Therapy), End User (Hospitals & Clinics and Research & Academic Institutes) and Region (Americas, Europe, Asia-Pacific and the Middle East & Africa) – Forecast till 2025
Pompe disease is a disorder affecting almost 1 in 40,000 people in the US. Factors such as constant uptake of long-term therapies, high cost of treatment, and launch of novel drugs are boosting the market growth. It is an autosomal recessive glycogen storage disorder and occurs due to deficiency of lysosomal enzyme acid α-glucosidase (GAA). The juvenile or adult-onset form and is reported to be the most common form in almost 80% of patients. This disorder primarily affects cardiac and skeletal muscle and manifests as progressive respiratory distress, skeletal muscles atrophy, and cardiomyopathy.
- Drug Suppliers
- Research and development (R&D) companies
- Government research laboratories
- Independent research laboratories
- Government and independent regulatory authorities
- Market research and consulting service providers
- Medical research laboratories
- Academic medical institutes and universities
The global Pompe disease treatment market by type has been segmented into onset Pompe disease, non-classic infantile-onset Pompe disease, and classic infantile-onset Pompe disease. Late-onset Pompe disease, a heterogeneous form of the disease, causes various problems related to musculoskeletal, neuromuscular, respiratory, and cardiac functioning. Late-onset Pompe disease mainly appears during teenage or adulthood. Late-onset is a progressive disease that causes weakness in muscles, spinal problem, cramps in legs, as well as headaches and fatigue in the patient. The late-onset segment is anticipated to capture the largest share of the global Pompe disease treatment market and is estimated to generate USD 844.7 million by 2025 at a CAGR of 2.7% from 2018.
The global Pompe disease treatment market, based on region, has been categorized as the Americas, Europe, Asia-Pacific, and the Middle East & Africa.
American regions are hubs for major market players operating in the Pompe disease treatment market, which eventually drives the growth of the American Pompe disease treatment market. Additionally, the rising awareness among the public about the available treatments for Pompe disease is projected to boost the market growth in America during the forecast period.
Europe stands second in the global Pompe disease treatment market followed by Asia-Pacific. European countries are extremely cautious and have implemented the new-born screening (NBS) program as a means of early detection and identification of severe illnesses in new-borns.
The prominent players in the global Pompe disease treatment market are Amicus Therapeutics, Inc., Genzyme Corporation, Audentes Therapeutics, Oxyrane, Valerion Therapeutics, AVROBIO, Inc., and CENTOGENE AG.
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